Elucidation of aberrant SBDS splicing mechanisms to design RNA-therapeutics for Shwachman-Diamond Syndrome
Balestra, Dario     dettagli >>

Anno: 2018

RNA-Based therapeutics for OTC deficiency
Balestra, Dario     dettagli >>

Anno: 2018

F8 splicing-swithcing molecules for tailored hemophilia A therapies
Balestra, Dario     dettagli >>

Anno: 2017